POSTER PRESENTATION AT WORLDSYMPOSIUM™ 2018 – ARIMOCLOMOL AS CLINICAL CANDIDATE FOR TREATMENT OF GAUCHER DISEASE
Copenhagen, February 6, 2018 – Orphazyme A/S, a Danish biotech company listed on Nasdaq Copenhagen (TICKER: ORPHA.CO), with a late-stage, orphan-drug pipeline, today announced that a poster on arimoclomol as a clinical candidate for the treatment of neuronopathic Gaucher disease will be presented at WORLDSymposium™ 2018 in San Diego, CA, USA.
PUBLICATION OF MANUSCRIPT RELATED TO PHASE II TRIAL RESULTS FOR ARIMOCLOMOL IN PATIENTS WITH SOD1 ALS
Copenhagen, January 24, 2018 – Orphazyme A/S, a Danish biotech company listed on Nasdaq Copenhagen (TICKER: ORPHA.CO), with a late-stage, orphan-drug pipeline, today announced that a manuscript reporting the Phase II trial results for arimoclomol in patients with SOD1 Amyotrophic Lateral Sclerosis (ALS) was published in the peer-reviewed clinical journal Neurology®. The manuscript highlights arimoclomol’s favorable safety profile and provides data on efficacy that supports the continued development of arimoclomol in a Phase II/III trial.
On December 14, 2017, Orphazyme A/S, University of Kansas Medical Center, and UCL announced that Orphazyme formally assumes the sponsorship of the Phase II/III arimoclomol trial for the neuromuscular disease sporadic Inclusion Body Myositis (sIBM).
ORPHAZYME RECEIVES ORPHAN DRUG DESIGNATION TO ARIMOCLOMOL FOR INCLUSION BODY MYOSITIS FROM THE U.S. FDA